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Showing posts with the label AAV Gene Therapies AAV Gene Therapies For Hemophilia B Treatment

AAV Gene Therapies: Revolutionizing Hemophilia B Treatment Landscape

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In recent years, the landscape of treating Hemophilia B has seen a revolutionary shift, primarily owing to the advent of AAV gene therapies. These therapies represent a promising avenue for addressing the inherent challenges in managing this rare bleeding disorder, offering hope for improved outcomes and a better quality of life for patients. HEMGENIX: The Only Approved Gene Therapy for Hemophilia B Treatment HEMGENIX , an AAV-based gene therapy, has emerged as a beacon of hope for Hemophilia B patients. It stands as the only approved gene therapy designed to address the underlying genetic cause of the disorder. By introducing a functional copy of the faulty gene responsible for clotting factor deficiency, HEMGENIX aims to provide sustained factor IX expression and reduce bleeding episodes significantly. Promising Gene Therapies in Pipeline for Hemophilia B Treatment The realm of Hemophilia B treatment is witnessing a surge in innovation, with several gene therapies in the pipeline. T