Fabry Disease Therapies on the Horizon
Fabry Disease: Epidemiology and Statistics Fabry Disease , a rare and debilitating genetic disorder, affects approximately 1 in 40,000 to 60,000 individuals worldwide. This X-linked condition primarily impacts males, although females can also experience symptoms. With a reported prevalence rate of about 1 in 1,500 to 1 in 117,000 among different populations, understanding Fabry Disease epidemiology is crucial for healthcare stakeholders. Current Fabry Disease Treatment Market Outlook and Persisting Unmet Needs Historically, Fabry Disease treatment aimed at managing symptoms and delaying organ damage. Enzyme replacement therapy (ERT) emerged as a game-changer, but it has limitations. ERTs require lifelong infusion, may not address all symptoms, and fail to halt disease progression in some patients. Subsequently, there is a persistent unmet need for more effective treatment options. Emerging Therapies and Their Place in Evolving Fabry Disease Treatment Approach Excitingly, the Fabry D