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Navigating the Complexities: Gene Therapies in Japan and the Road to Effective Reimbursement

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The field of regenerative medicine has witnessed remarkable advancements in recent years, particularly in the areas of cell therapy and gene therapy . Japan, with its strong focus on regenerative medicine, has emerged as a key company in cell therapy and gene therapy . However, while cell therapies have found success in Japan, the journey for gene therapies has been more complex. In this blog, we explore the current landscape and challenges surrounding cell and gene therapies in Japan. Novartis' ZOLGENSMA: The Only Approved Gene Therapy in Japan Novartis' ZOLGENSMA , a groundbreaking gene therapy for the treatment of spinal muscular atrophy (SMA), has received approval in Japan. This landmark approval marked a watershed moment for gene therapies in the country. ZOLGENSMA offers hope to patients and their families, as it addresses the root cause of the disease, offering potential long-term benefits. The successful introduction of ZOLGENSMA paves the way for future gene therapies